At Ionis, we’re passionate about supporting and educating patients and their families because we know that daily life with a serious disease can be extremely challenging.
Because we’re focused on serving the needs of patients across a wide variety of diseases, we collaborate with various partners, patient advocacy organizations and societies who share similar goals to make sure that patients get the support and resources they need.
Patient Resources
Severe Hypertriglyceridemia and Familial Chylomicronemia Syndrome
Transthyretin Amyloidosis
Angelman Syndrome
Alexander Disease
MECP2 Duplication Syndrome
Huntington’s Disease
Pelizaeus-Merzbacher Disease (PMD)
Prion Disease
Spinal Muscular Atrophy
Hereditary Angioedema (HAE)
Ionis Clinical Trials
Receiving a devastating diagnosis can be overwhelming, especially when there are no approved therapies available and limited information to be found. We have many ongoing clinical trials evaluating our investigational medicines in a variety of disease areas including cardiovascular, neurologic, and rare diseases.
