Neurology
ION337 Data Presented at the American Society of Nephrology (ASN) Kidney Week 2026
Scientific Publications & Presentations
Built on decades of scientific leadership, Ionis continues to advance the understanding of disease through groundbreaking research and innovation. Explore select publications across our therapeutic areas and technologies to better understand the science behind our medicines and pipeline.
Showing 1-12 out of 49 results
Neurology
Developmental skills and adaptive functioning in MECP2 duplication syndrome
Neurology
Diranersen Data Presented at the Alzheimer's Association International Conference (AAIC) 2026
Neurology
PrP turnover in vivo and the time to effect of prion disease therapeutics
Neurology
Enhanced splicing modulation by NMA-modified antisense oligonucleotides
Neurology
Salanersen Data Presented at the Muscular Dystrophy Association (MDA) Clinical & Scientific Conference
Castro et al - Phase 1 interim results evaluating the safety tolerability pharmacokinetics and exploratory efficacy of salanersen for spinal muscular atrophy.pdf
Crawford et al - STELLAR Phase 3 Studies to Evaluate the Efficacy and Safety of Salanersen in Infants with Spinal Muscular Atrophy.pdf
Shieh et al - The SOLAR Study - Phase 3 Study to Evaluate the Efficacy and Safety of Salanersen in Participants Aged 15 to 60 Years with Spinal Muscular Atrophy.PDF
Neurology
Exploratory analyses of clinical outcomes from the BIIB080 phase 1b study in mild Alzheimer’s disease
Neurology
High-dose nusinersen for spinal muscular atrophy: a phase 3 randomized trial
Neurology
Long-Term Tofersen in SOD1 Amyotrophic Lateral Sclerosis
Neurology
A single-arm phase 2 trial of an investigational RNA therapeutic to complement factor B sefaxersen for treatment of IgA nephropathy
Neurology
ION582 Data Presented at the 2025 FAST Conference
Neurology
ION717 Data Presented at the Prion 2025 Congress