Neurology
Antisense suppression of glial fibrillary acidic protein as a treatment for Alexander disease
Scientific Publications & Presentations
Built on decades of scientific leadership, Ionis continues to advance the understanding of disease through groundbreaking research and innovation. Explore select publications across our therapeutic areas and technologies to better understand the science behind our medicines and pipeline.
Showing 49-51 out of 51 results
Neurology
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
Neurology
Towards a therapy for Angelman syndrome by targeting a long non-coding RNA