Neurology
Pelizaeus-Merzbacher Disease: A Caregiver Assessment of Disease Impact
Scientific Publications & Presentations
Built on decades of scientific leadership, Ionis continues to advance the understanding of disease through groundbreaking research and innovation. Explore select publications across our therapeutic areas and technologies to better understand the science behind our medicines and pipeline.
Showing 73-84 out of 104 results
Other Medicines
TMPRSS6 as a Therapeutic Target for Disorders of Erythropoiesis and Iron Homeostasis
Neurology
Antisense oligonucleotide therapy rescues disturbed brain rhythms and sleep in juvenile and adult mouse models of Angelman syndrome
Other Medicines
Efficacy and Safety of Bepirovirsen in Chronic Hepatitis B Infection
Neurology
Liver-directed drugs for transthyretin-mediated amyloidosis
Neurology
Trial of Antisense Oligonucleotide Tofersen for SOD1 ALS
Neurology
Eplontersen Data Presented at the XVIII International Symposium on Amyloidosis
Other Medicines
Antisense oligonucleotides ameliorate kidney dysfunction in podocyte-specific APOL1 risk variant mice
Other Medicines
Inhibition of Prekallikrein for Hereditary Angioedema
Cardiometabolic Disease
Antisense Therapy Attenuates Phospholamban p.(Arg14del) Cardiomyopathy in Mice and Reverses Protein Aggregation
Other Medicines
Tmprss6-ASO as a tool for the treatment of Polycythemia Vera mice
Neurology
Antisense therapy in a rat model of Alexander disease reverses GFAP pathology, white matter deficits, and motor impairment