Neurology
Tau-targeting antisense oligonucleotide MAPTRx in mild Alzheimer's disease: a phase 1b, randomized, placebo-controlled trial
Scientific Publications & Presentations
Built on decades of scientific leadership, Ionis continues to advance the understanding of disease through groundbreaking research and innovation. Explore select publications across our therapeutic areas and technologies to better understand the science behind our medicines and pipeline.
Showing 25-36 out of 39 results
Neurology
Antisense oligonucleotide therapy rescues disturbed brain rhythms and sleep in juvenile and adult mouse models of Angelman syndrome
Other Medicines
Efficacy and Safety of Bepirovirsen in Chronic Hepatitis B Infection
Neurology
Liver-directed drugs for transthyretin-mediated amyloidosis
Neurology
Trial of Antisense Oligonucleotide Tofersen for SOD1 ALS
Neurology
Eplontersen Data Presented at the XVIII International Symposium on Amyloidosis
Other Medicines
Inhibition of Prekallikrein for Hereditary Angioedema
Neurology
Antisense therapy in a rat model of Alexander disease reverses GFAP pathology, white matter deficits, and motor impairment
Neurology
Angelman syndrome genotypes manifest varying degrees of clinical severity and developmental impairment
Neurology
Phase 1–2 Trial of Antisense Oligonucleotide Tofersen for SOD1 ALS
Neurology
Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
Neurology
Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy